Pembrolizumab (Keytruda) for Stage IV Cancer

Also known as: Keytruda, MK-3475

The most widely prescribed checkpoint inhibitor, pembrolizumab has revolutionized treatment across 30+ cancer types by unleashing anti-tumor immunity.

Mechanism of Action

Pembrolizumab is a humanized IgG4 monoclonal antibody that blocks PD-1 receptor on T cells, preventing engagement with PD-L1/PD-L2 ligands on tumor cells. This removes the 'immune brake,' restoring cytotoxic T cell function against tumor-associated antigens. Response correlates with PD-L1 expression, tumor mutational burden, and microsatellite instability.

General mechanism: Anti-PD-1 monoclonal antibody. Blocks immune checkpoint to restore T cell anti-tumor activity.

Current Evidence

Landmark trials across NSCLC, melanoma, head and neck, urothelial, gastric, cervical, and MSI-high cancers show durable responses in 20-40% of patients. KEYNOTE program has generated the largest immunotherapy dataset. Combination with chemotherapy improves first-line response rates.

Clinical Status: FDA-approved for 30+ indications. First-line standard of care for PD-L1+ NSCLC, melanoma, and many others. Over $25B annual revenue reflects clinical impact.

Safety Profile

Immune-related adverse events (colitis, pneumonitis, hepatitis, endocrinopathies) in 15-30% of patients. Most manageable with corticosteroids. Rare but serious: myocarditis, encephalitis.

Key Research Questions

View glossary entry →

← Back to Stage IV Cancer Research